Gene therapy: Gene fix does not prevent cell loss

Nature 493, 7434 (2013). doi:10.1038/493581c

Gene therapy improves the vision of people with a genetic form of blindness, but does not stop the loss of the light-sensitive photoreceptor cells in the retina.Childhood blindness as a result of Leber congenital amaurosis (LCA) occurs as a result of photoreceptor dysfunction and (Source: Nature)MedWorm Sponsor Message: Find the best Christmas presents and January Sales in the UK with this simple shopping directory.
Source: Blindness